Friedrich K. Trefz,
Barbara K. Burton,
Nicola Longo,
Mercedes Martinez-Pardo Casanova,
Daniel J. Gruskin,
Alex Dorenbaum,
Emil D. Kakkis,
Eric A. Crombez,
Dorothy K. Grange,
Paul Harmatz,
Mark H. Lipson,
Andrzej Milanowski,
Linda Marie Randolph,
Jerry Vockley,
Chester B. Whitley,
Jon A. Wolff,
Judith Bebchuk,
Heidi Christ-Schmidt,
Julia B. Hennermann,
- Efficacy of sapropterin dihydrochloride in increasing phenylalanine tolerance in children with phenylketonuria: a phase III, randomized, double-blind, placebo-controlled study. Trefz, F.K., Burton, B.K., Longo, N., Casanova, M.M., Gruskin, D.J., Dorenbaum, A., Kakkis, E.D., Crombez, E.A., Grange, D.K., Harmatz, P., Lipson, M.H., Milanowski, A., Randolph, L.M., Vockley, J., Whitley, C.B., Wolff, J.A., Bebchuk, J., Christ-Schmidt, H., Hennermann, J.B. J. Pediatr. (2009)